The families of the 1 in 20 kids facing a birth defect or genetic disease are used to hearing words like “incurable” or “lifelong effects”. It doesn’t have to be this way. Right now, we’re working on gene therapy to find cures for previously incurable genetic diseases.

Kids just want to be kids, but instead of playing sports with their friends or catching butterflies on a sunny day, these kids are getting liver transplants, taking dozens of medications, or getting their next dose of chemotherapy.

Your support helps the scientists at Children’s Medical Research Institute find cures, so these kids and millions more like them can go back to being kids. Thank you!